Author: William Jeffery

RARE – Ultragenyx: A Promising Bet On Rare Genetic Disorder Therapies

African ethnicity scientists studying DNA samples. Computer screens with DNA sequences. Discussing


In the rapidly-evolving landscape of biopharmaceuticals, one company that stands out for its highly focused and promising approach to addressing rare genetic diseases is Ultragenyx Pharmaceutical Inc. (NASDAQ:RARE). The company’s financials demonstrate remarkable resilience, with astute expense management, robust cash

DYN – Dyne Therapeutics: FORCE Platform Poised To Revolutionize Gene Therapy

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Dyne Therapeutics, Inc. (NASDAQ:DYN) is a clinical-stage muscle disease company that is positioned to transform the lives of individuals living with genetically driven muscle diseases through its innovative oligonucleotide therapeutics. The company’s proprietary FORCE platform overcomes the